This website is intended for residents of the U.S. interested in achondroplasia or VOXZOGO

Staying the course with your routine

Treatment tips as your family’s needs change

Establish your reason for choosing VOXZOGO to keep you and your family committed for the duration of treatment. Build confidence with your child to help start and continue their treatment routine.

Chat with another caregiver who is raising a child with achondroplasia.

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Identify goals and appropriate expectations with your doctor

Set goals for what you and your family hope to get out of treatment. Revisit them as your child progresses.

Every child is unique and may respond to treatment differently.

Lean on your Clinical Coordinator

You will be paired with a
BioMarin Clinical Coordinator who will provide ongoing product education and support throughout the duration of your child’s treatment.

Track progress through growth and weight check-ups

It’s typical to see results after 1-2 years of starting treatment. Children’s growth rates
naturally vary over time. While on VOXZOGO, your child’s growth rate may slow down or stay the same over a period of time, but this does not mean it is not working.

Continue to celebrate every milestone and reflect on why you decided to start treatment.

Meet with your doctor regularly

Your child’s appointments are a great opportunity to ask questions and have open, productive conversations about treatment. Work with your child’s doctor to:

  • Get measurements taken every 3 to 6 months and reference against achondroplasia-specific growth charts
  • Get growth-specific monitoring from a specialist, such as a pediatric endocrinologist or geneticist

Support right from the start

Experience one-to-one support and assistance throughout treatment.

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Meet families like yours

The VOXZOGO Mentor Program pairs you with a caregiver raising a child on VOXZOGO.

Connect With a Caregiver

Looking for more information about VOXZOGO?

Your local BioMarin representative can help you find answers.

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Connect With a Rep

IMPORTANT SAFETY INFORMATION

What is the most important safety information about VOXZOGO?

  • VOXZOGO may cause serious side effects including a temporary decrease in blood pressure in some patients. To reduce the risk of a decrease in blood pressure and associated symptoms (dizziness, feeling tired, or nausea), patients should eat a meal and drink 8 to 10 ounces of fluid within 1 hour before receiving VOXZOGO.

What are the most common side effects of VOXZOGO?

  • The most common side effects of VOXZOGO include injection site reactions (including redness, itching, swelling, bruising, rash, hives, and injection site pain), high levels of blood alkaline phosphatase shown in blood tests, vomiting, joint pain, decreased blood pressure, and stomach ache. These are not all the possible side effects of VOXZOGO. Ask your healthcare provider for medical advice about side effects, and about any side effects that bother the patient or that do not go away.

How is VOXZOGO taken?

  • VOXZOGO is taken daily as an injection given under the skin, administered by a caregiver after a healthcare provider determines the caregiver is able to administer VOXZOGO. Do not try to inject VOXZOGO until you have been shown the right way by your healthcare provider. VOXZOGO is supplied with Instructions for Use that describe the steps for preparing, injecting, and disposing VOXZOGO. Caregivers should review the Instructions for Use for guidance and any time they receive a refill of VOXZOGO in case any changes have been made.
  • Inject VOXZOGO 1 time every day, at about the same time each day. If a dose of VOXZOGO is missed, it can be given within 12 hours from the missed dose. After 12 hours, skip the missed dose and administer the next daily dose as usual.
  • The dose of VOXZOGO is based on body weight. Your healthcare provider will adjust the dose based on changes in weight following regular check-ups.
  • Your healthcare provider will monitor the patient’s growth and tell you when to stop taking VOXZOGO if they determine the patient is no longer able to grow. Stop administering VOXZOGO if instructed by your healthcare provider.

What should you tell the doctor before or during taking VOXZOGO?

  • Tell your doctor about all of the patient’s medical conditions including
    • If the patient has heart disease (cardiac or vascular disease), or if the patient is on blood pressure medicine (anti-hypertensive medicine).
    • If the patient has kidney problems or renal impairment.
    • If the patient is pregnant or plans to become pregnant. It is not known if VOXZOGO will harm the unborn baby.
    • If the patient is breastfeeding or plans to breastfeed. It is not known if VOXZOGO passes into breast milk.
  • Tell your doctor about all of the medicines the patient takes, including prescription and over-the-counter medicines, vitamins, and herbal supplements.

You may report side effects to BioMarin at 1-866-906-6100. You are encouraged to report negative side effects of prescription drugs to the FDA. Visit www.fda.gov/medwatch, or call 1-800-FDA-1088.

Please see additional safety information in the full Prescribing Information and Patient Information.

What is VOXZOGO used for?

  • VOXZOGO is a prescription medicine used to increase linear growth in children with achondroplasia and open growth plates (epiphyses).
  • VOXZOGO is approved under accelerated approval based on an improvement in annualized growth velocity. Continued approval may be contingent upon verification and description of clinical benefit in confirmatory trials.