This website is intended for residents of the U.S. interested in achondroplasia or VOXZOGO

Meet families who chose VOXZOGO

Treatment stories from the achondroplasia community

Families who started VOXZOGO early

Sophie, 9 months old, on VOXZOGO since 3 months old

Meet Sophie and listen as her mom, Amanda, shares why she feels she made the right decision for her family to start Sophie on VOXZOGO at 3 months old.

Eve, 3 years old, on VOXZOGO since 16 months old as part of a clinical trial

Get to know Eve and hear her mom, Julie, talk about why she decided to start VOXZOGO as early as possible.

Shawn, 8 years old, on VOXZOGO since 4 years old as part of a clinical trial

Meet Shawn and hear from his mom, Patty, as she discusses how important their BioMarin Clinical Coordinator was to helping their family understand, start, and feel supported throughout treatment.

Families who have made VOXZOGO a part of their daily routine

Miller, 13 years old, on VOXZOGO since 10 years old as part of a clinical trial

Hear Miller and his parents describe how they got their family used to an injection routine.

Annika, 14 years old, on VOXZOGO since 9 years old as part of a clinical trial

See Annika and her mom, Krista, share their story about how they decided to start and stay on VOXZOGO.

Families who have completed VOXZOGO

Vivan, 18 years old, started VOXZOGO at 8 years old until his growth plates closed as part of a clinical trial

Watch Vivan discuss his passion for playing basketball and describe how he stayed dedicated to his treatment routine.

Satya, Vivan’s dad

Hear Satya share why his family decided VOXZOGO was the right choice for Vivan and why they feel it’s important to start as early as possible.

Ahmin, 17 years old, completed treatment with VOXZOGO

Learn how Ahmin built a routine over time that helped him stay the course throughout his treatment experience.

Munira, Ahmin’s mom

Munira shares how she became a strong advocate for her son since his birth, including throughout his VOXZOGO journey.

More than 5,000 families worldwide have chosen
VOXZOGO for their infants and children with achondroplasia

Meet families like yours

The VOXZOGO Mentor Program pairs you with a caregiver raising a child on VOXZOGO.

Connect With a Caregiver

Looking for more information about VOXZOGO?

Your local BioMarin representative can help you find answers.

Connect Now

Connect With a Rep

IMPORTANT SAFETY INFORMATION

What is the most important safety information about VOXZOGO?

  • VOXZOGO may cause serious side effects including a temporary decrease in blood pressure in some patients. To reduce the risk of a decrease in blood pressure and associated symptoms (dizziness, feeling tired, or nausea), patients should eat a meal and drink 8 to 10 ounces of fluid within 1 hour before receiving VOXZOGO.

What are the most common side effects of VOXZOGO?

  • The most common side effects of VOXZOGO include injection site reactions (including redness, itching, swelling, bruising, rash, hives, and injection site pain), high levels of blood alkaline phosphatase shown in blood tests, vomiting, joint pain, decreased blood pressure, and stomach ache. These are not all the possible side effects of VOXZOGO. Ask your healthcare provider for medical advice about side effects, and about any side effects that bother the patient or that do not go away.

How is VOXZOGO taken?

  • VOXZOGO is taken daily as an injection given under the skin, administered by a caregiver after a healthcare provider determines the caregiver is able to administer VOXZOGO. Do not try to inject VOXZOGO until you have been shown the right way by your healthcare provider. VOXZOGO is supplied with Instructions for Use that describe the steps for preparing, injecting, and disposing VOXZOGO. Caregivers should review the Instructions for Use for guidance and any time they receive a refill of VOXZOGO in case any changes have been made.
  • Inject VOXZOGO 1 time every day, at about the same time each day. If a dose of VOXZOGO is missed, it can be given within 12 hours from the missed dose. After 12 hours, skip the missed dose and administer the next daily dose as usual.
  • The dose of VOXZOGO is based on body weight. Your healthcare provider will adjust the dose based on changes in weight following regular check-ups.
  • Your healthcare provider will monitor the patient’s growth and tell you when to stop taking VOXZOGO if they determine the patient is no longer able to grow. Stop administering VOXZOGO if instructed by your healthcare provider.

What should you tell the doctor before or during taking VOXZOGO?

  • Tell your doctor about all of the patient’s medical conditions including
    • If the patient has heart disease (cardiac or vascular disease), or if the patient is on blood pressure medicine (anti-hypertensive medicine).
    • If the patient has kidney problems or renal impairment.
    • If the patient is pregnant or plans to become pregnant. It is not known if VOXZOGO will harm the unborn baby.
    • If the patient is breastfeeding or plans to breastfeed. It is not known if VOXZOGO passes into breast milk.
  • Tell your doctor about all of the medicines the patient takes, including prescription and over-the-counter medicines, vitamins, and herbal supplements.

You may report side effects to BioMarin at 1-866-906-6100. You are encouraged to report negative side effects of prescription drugs to the FDA. Visit www.fda.gov/medwatch, or call 1-800-FDA-1088.

Please see additional safety information in the full Prescribing Information and Patient Information.

What is VOXZOGO used for?

  • VOXZOGO is a prescription medicine used to increase linear growth in children with achondroplasia and open growth plates (epiphyses).
  • VOXZOGO is approved under accelerated approval based on an improvement in annualized growth velocity. Continued approval may be contingent upon verification and description of clinical benefit in confirmatory trials.